For over 20 years scientists and researchers have been investigating ways gene therapy can both treat or prevent genetic diseases; attempting to treat the disease at the molecular level by correcting mistakes at the gene level.
The 80’s kicked off the Human Genome Project. Completed in it's entirety in 2003 the project identified and mapped all genes from the human genome. With this, researchers are more easily able to identify target genes.
By the early 90’s the first gene therapy was being delivered to newborn patients with ADA deficiency (adenosine deaminase deficiency, ADA-SCID) a rare metabolic disease.
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